AveXis Clinical Trial for Infants Aged Less than Six Months Old with SMA Type 1 in the UK
27 September 2018
This Phase 3 study called STR1VE-EU, will evaluate the safety and efficacy of a one-time intravenous infusion of AVXS-101 in approximately 30 European infants.
Avexis’ community update with details of the study is here.
Great Ormond Street Hospital is actively screening infants. Contact Hinal Patel:
- phone 0207 905 2602 ext. 42602
- email hinal.patel@ucl.ac.uk
The John Walton Muscular Dystrophy Centre for Research in Newcastle will be activated very soon. Contact Anna Peel:
- phone 0191 241 8649
- email Anna.peel1@newcastle.ac.uk