SMA UK Busy Heading Out and About

13 November 2018

SMA UK have been busy heading out and about recently; last week, along with Muscular Dystrophy UK, we were patient representatives at NICE’s scoping meeting for AVXS-101 for SMA Type 1. You can read more about AVXS-101 here

We also attended Genetic Alliance UK’s workshop for rare disease groups discussing a Patient Charter for Newborn Screening in the UK.