Clinical Care Research

Clinicians worldwide are constantly working on how to manage the symptoms and provide the highest standards of care so that people with SMA can have the best possible quality of life. 

Physiotherapy - Based Measures (HINE, CHOP INTEND, HMFSE) for People with SMA and how they are used to Monitor Treatment Outcomes

Physiotherapy - Based Measures (HINE, CHOP INTEND, HMFSE) for People with SMA and how they are used to Monitor Treatment Outcomes

Our Clinical Care Research Correspondent, Dr ALex Murphy, has been discussing, with Dr Anna Mayhew (Consultant Research Physiotherapist at Newcastle), some of the more commonly used outcome measures in SMA. Together, they have produced the following summary.

Long-Term Assessment of Salbutamol in SMA Type 3

Long-Term Assessment of Salbutamol in SMA Type 3

This latest article from our Clinical Care Research Correspondent, Dr Alex Murphy, discusses how Tiziano and colleagues studied individuals with SMA taking salbutamol over a one year period.

Scoliosis in Spinal Muscular Atrophy

Scoliosis in Spinal Muscular Atrophy

This article looks at recent research into different aspects of spinal surgery, in the treatment of scoliosis in Spinal Muscular Atrophy.

ENMC Workshop - 'Airway clearance techniques in Neuromuscular Disorders'

ENMC Workshop - 'Airway clearance techniques in Neuromuscular Disorders'

On 3rd March 2017, 21 participants from 12 countries across the world met in Naarden, Netherlands, to attend and contribute to this 228th ENMC International Workshop. You can read a journal report of this workshop here.

What Happens After a Successful Clinical Trial?

What Happens After a Successful Clinical Trial?

In this article, Dr. Alex Murphy - our Clinical Care Research Correspondent - describes the organisations involved and outlines the processes that have to be gone through before a drug can be prescribed for an individual in the UK.

Complementary and Alternative Therapies in SMA

Complementary and Alternative Therapies in SMA

In Dr. Alex Murphy's latest article, he summaries some of the more common CATs (Complementary and Alternative Therapies) and looks into evidence for their use in SMA or similar conditions.

End Of Life Care

End Of Life Care

In this article, Dr. Alex Murphy describes the sensitivity of discussions around 'end of life care'. He also introduces some of the studies that have been carried out to examine the effectiveness of palliative care.

Medications Research Review

Medications Research Review

Dr. Alex Murphy, looks at medications that target other conditions that have been investigated as a treatment for SMA. He gives some background on each medicine, how they are supposed to work and how the medicine was investigated in clinical trials.

How Do Doctors Select Treatments?

How Do Doctors Select Treatments?

In this article, Dr Alex Murphy will try to answer this question and outline one way that decision makers within the NHS compare the different types of study and decide on how strong the evidence is, for or against a treatment.

Diet and Spinal Muscular Atrophy

Diet and Spinal Muscular Atrophy

In this review article, Dr Alex Murphy, our Clinical Care Research Correspondent, highlights and explains what research has looked into nutrition and SMA over the past three years.