UK SMA RESEARCH CONSORTIUM – A UK-WIDE COLLABORATIVE NETWORK

Principal Investigator(s): Professor Kevin Talbot & Professor Tom Gillingwater

Institution: The Universities of Oxford

Funding: £1,327,199

Year awarded: 2016

Status: Ongoing

The UK SMA Consortium consists of 6 world-class research teams based in Oxford, Edinburgh, Sheffield and London. The teams are working collaboratively across 4 main areas:

  1. Exploring the ways in which SMA affects different organs/systems within the body and which might be targets for treatments
  2. Looking at what treatments could be beneficial if used in combination with current SMN-boosting drugs like nusinersen (Spinraza)
  3. Developing models to test out potential treatments
  4. Looking at new methods of drug delivery including in the womb