SMA Drug Pipeline

Using this drug pipeline, we are tracking the development of all possible SMA treatments currently being tested in human clinical trials.

The diagram is split into:

  • drugs that increase SMN protein levels (SMN-dependent)
  • drugs that do not affect SMN protein levels (SMN-independent)

Download the diagram below to see how far development of each drug has progressed and follow links to further information about each drug on our website. You can also find listings for any related global trial on the website, if applicable. Each listing includes details such as eligibility criteria, where in the world the trial is taking place and whether the trial is currently recruiting.

The diagram will be regularly updated to map the development and progress of each drug programme.

Download the diagram

Last updated April 2022