SMA UK's & MDUK’s Joint Submission to NICE Re: Risdiplam

This submission was to NICE as to whether they should recommend that NHS England funds Risdiplam.

Thank you to those of you who completed the survey we ran about your views on this. They were crucial for the submission we made.

The first committee meeting is scheduled for 11th May 2021.

Below are the links to see the submission and accompanying documents:

Joint submission

Appendix 1 - Survey Summary Tables of All Respondents

Appendix 2 - Survey Summary Tables of Adult Respondents

Appendix 3 - Survey Summary Tables of Parents of Children under 18 years

Appendix 4 - Comments from the survey

Appendix 5 - Risdiplam Summary

Appendix 6 - Risdiplam Trial Summary

Appendix 7 - Survey respondents in England who are receiving nusinersen