APPG for Muscular Dystrophy: Newborn Screening for Rare Conditions
Information
Information
Novartis presents data on long-term treatment with Zolgensma
Taldefgrobep Alfa Receives FDA Fast Track Designation for SMA
ROCHE Community Update – SUNFISH Trial
NHS England Provides Further Guidance around Definition of Non-Success of Zolgensma
Results Published from STRONG Trial of Zolgensma
Conversations with health professionals – new webinar!
SEND and Alternative Provision Improvement Plan published
Interim Results from Risdiplam Jewelfish Trial Published
NHS England agrees to allow access to Sapphire Trial to enhance treatments for SMA
