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Newborn Screening for SMA

two people in science laboratory, female scientist looking down microscope

Advocacy for Treatments

child, young adult and adult all with SMA

Social Care, Education, Work & Transport

Image shows an adult man, who has SMA, sitting in his wheelchair holding an ice cream in one hand, and a drink in the other.

Priorities for Adults

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SMA Awareness

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Rare Diseases Collaborations