This latest article from our Clinical Care Research Correspondent, Dr Alex Murphy, discusses how Tiziano and colleagues studied individuals with SMA taking salbutamol over a one year period.
Read full storyGenetic Alliance UK are working on a policy project to improve access to medicines for rare diseases, called Resetting the Model. They have launched a survey to understand your views on how decisions should be made around access to rare disease medicines.
Read full storyScholar Rock have announced positive interim results from an ongoing Phase I trial in healthy volunteers of their lead compound, SRK-015.
Read full storyThis study involves an online survey for people aged 18 or over who either have a genetic condition themselves, or have someone in their family who has / had a genetic condition. It's being led by University College London with a closing date of 30th May.
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