Risdiplam (Evrysdi)
Risdiplam (Evrysdi)
Last updated: 15th July 2026
Risdiplam clinical trials and their results
Researchers have tested risdiplam in human clinical trials since 2015. Risdiplam is not a cure for 5q SMA but in these trials, it has been consistently shown to have an acceptable safety profile and to be well-tolerated. When compared to no treatment, it has led to clinically meaningful improvements in muscle function. Several trials of risdiplam are still ongoing.
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