The development of all possible SMA treatments being tested in human clinical trials.
Information on accessing treatment in the UK and information for those living overseas.
SMA treatments in the pipeline and drugs currently being tested in clinical trials.
Access to Biogen’s drug for those who meet the eligibility criteria.
Access to Roche’s drug for those who meet the eligibility criteria.
Access to Novartis’ drug for children who have SMA Type 1 and meet the eligibility criteria.
The tools and measures that may be used as part of collecting information about a drug’s clinical effectiveness.
New and ongoing projects that have been taking place.
Different approaches that have reached human clinical trial stages.
