Scotland – Access to Nusinersen

Page last checked: 17th December 2024

Nusinersen is routinely available to children who have SMA Type 1.

In July 2019, access was expanded to include all those who have SMA Types 2 or 3. This was under the ultra-orphan pathway further evidence on its effectiveness is gathered.

Access for Children

These paediatric centres offer assessment for and treatment with nusinersen:

Royal Aberdeen Children’s Hospital
Nine Wells Hospital – Dundee
Royal Hospital for Sick Children Edinburgh
Royal Hospital for Children Glasgow

Our summary guide discussing all the potential treatments may be useful: Drug Treatments for Children who have 5qSMA.

Our Conversations with Health Professionals webinars include latest updates on treatment.

Access for Adults

There are currently no centres offering this service for adults in Scotland. If you want to pursue the possibility of nusinersen treatment we suggest you talk to the clinical team at your nearest centre. The Scottish Muscle Network is another possible source of advice.

Our summary guide discussing all the potential treatments may be useful: Drug Treatments for Adults who have 5qSMA.

Our Conversations with Health Professionals webinars include latest updates on treatment.