Page last checked: 29th November 2022
Last updated: 17th March 2023

Nusinersen is routinely available to children who have SMA Type 1.

Since July 2019, it can be prescribed for all those who have SMA Types 2 or 3 under the ultra-orphan pathway for a period of up to three years while further evidence on its effectiveness is generated.

In Scotland, the following paediatric centres offer assessment for and treatment with nusinersen:

• Royal Aberdeen Children’s Hospital
• Nine Wells Hospital – Dundee
• Royal Hospital for Sick Children Edinburgh
• Royal Hospital for Children Glasgow

Our summary guide Drug Treatments for Children in England who have SMA provides information that may be helpful wherever you live.

There are currently no centres offering this service for adults in Scotland. If you want to pursue the possibility of nusinersen treatment we suggest you talk to the clinical team at your nearest centre. The Scottish Muscle Network is another possible source of advice.

Our summary guide Drug Treatments for Adults in England who have SMA provides information that may be helpful wherever you live.

Nusinersen is now moving into Stage 3 Evidence Generation as described in the SMC guidance about the ultra-orphan pathway.

Read more about our work to progress access to nusinersen in Scotland, here.