SMA Drug Pipeline
SMA Drug Pipeline
Page last updated: May 2024
Using this drug pipeline, we are tracking the progress of SMA treatments currently being tested in human clinical trials.
The diagram is split into:
- drugs that increase SMN protein levels (SMN-dependent)
- combined treatments that deliver SMN-dependent with SMN-independent drugs (those that do not affect SMN protein levels)
- SMN-independent treatments that aim to support the neuromuscular system
Download the diagram below to see how each drug is progressing through clinical trials and follow links to further information about each drug. You can also find listings for any related global trial on the ClinicalTrials.gov website. Each listing includes details such as:
- eligibility criteria
- where in the world the trial is taking place
- if the trial is currently recruiting.
The diagram will be regularly updated to map the development and progress of each drug programme.
Download the drug pipeline diagram >
Researchers have tested other drugs in clinical trials. As a result they have then found them not suitable for treating SMA: