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Although there’s currently no cure for SMA, drug treatments are now available.

These pages tell you about any NHS-funded drug treatments, any in the pipeline, and other related topics. Whatever the treatment, it remains vital that anyone who has SMA also has appropriate care and management based on assessment by and discussion with their clinical team. Though some recommendations are now changing, the internationally agreed Standards of Care for SMA remains a useful reference point.

Major concerns over the future of adult neuromuscular care in Northern Ireland

Information
Treatments & Research

Updated guidance on Risdiplam

Information
News
Treatments & Research

Roche Provides End of Year Community Update

Information
Treatments & Research
Image shows the Roche logo in white on a dark blue background.

Republic of Ireland adds SMA to the newborn screening blood spot test!

News
Information
Treatments & Research

Progress update on UK NSC work to assess newborn screening for SMA

Advocacy
Information
News
Treatments & Research

Eating, Diet and Nutrition in SMA

Information
Treatments & Research

SMA on the first list of conditions screened for in Genomics England‘s Generation Study

News
Advocacy
Treatments & Research

Planning for a UK-wide SMA newborn screening pilot to start later this year

Advocacy
News
Treatments & Research

NICE preparing for the review of Nusinersen and Risdiplam 

Treatments & Research
News

Spinal Muscular Atrophy: A Rare but Treatable Disease of the Nervous System

News
Treatments & Research