Visit to the Wolfson Centre for Personalised Medicine: Advancing SMA Treatment Safety
Treatments & Research
Treatments & Research
Although there’s currently no cure for SMA, drug treatments are now available.
These pages tell you about any NHS-funded drug treatments, any in the pipeline, and other related topics. Whatever the treatment, it remains vital that anyone who has SMA also has appropriate care and management based on assessment by and discussion with their clinical team. Though some recommendations are now changing, the internationally agreed Standards of Care for SMA remains a useful reference point.
Update on NICE Decision for Continued Access to risdiplam (Evrysdi) and nusinersen (Spinraza).
Landmark victory as Spinraza becomes routinely available on the NHS in Scotland
Hattie and James share their son Theo’s story about his SMA diagnosis
SMA Care UK – one year on
Bringing SMA Care UK into focus at the annual conference of British Neurologists
SMA UK lead on collating and submitting comments on the MTA EAG report in collaboration with Treat SMA and MDUK.
SMA UK at the International Scientific Congress on SMA 2024
Roche Provides Community Update on Risdiplam Data, including Tablet Formulation
