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Results Published from STRONG Trial of Zolgensma

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Giles Lomax – CEO Announcement

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Giles Lomax

Conversations with health professionals – new webinar!

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New families’ Whatsapp group launched!

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SEND and Alternative Provision Improvement Plan published

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Say hi to Martin!

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Interim Results from Risdiplam Jewelfish Trial Published

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NHS England agrees to allow access to Sapphire Trial to enhance treatments for SMA

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England’s Managed Access Agreement for Nusinersen extended to July 2025

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Scholar Rock presents latest TOPAZ Trial data at the international scientific congress on SMA

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