5-Year Results from the Nurture Spinraza Trial Published
News & Updates
News & Updates
Scholar Rock Provide Update on Phase 2 TOPAZ trial of Apitegromab
We are excited to share with you our brand refresh and new website!
Ian, Mark, Neil & Paul’s LEJOG Challenge
Taking the leap for SMA UK
Say hello to Gary!
APPG for Muscular Dystrophy: Newborn Screening for Rare Conditions
SMA UK Trustee Event – An evening with Sir Richard Dearlove OBE
Calling for Progress on Care Coordination in the UK
Novartis presents data on long-term treatment with Zolgensma
