Making Care Better: SMA UK’s Fight for Change
News & Updates
News & Updates
Itvisma from Novartis, a new, safer way of administering gene therapy for older children and adults living with SMA
Update on NICE Decision for Continued Access to risdiplam (Evrysdi) and nusinersen (Spinraza).
First NICE committee meeting for continued access to Spinraza and Risdiplam
Challenging the Flawed Baseline: Why SMA Treatment Must Offer Choice, Not Just “Supportive Care”.
The Power of Real-World Data: Why Patients’ Experiences Prove the Case for SMA Drugs
Beyond Mobility: Why Holding the Line is a Major Win in SMA Treatment
Landmark victory as Spinraza becomes routinely available on the NHS in Scotland
The Scottish Government will be adding SMA to their newborn screening programme
Newborn Screening Committee publish a breakdown of evidence for SMA screening.
