Our Advocacy and Progress Towards Nusinersen Access in the UK

NICE review of of Nusinersen and Risdiplam (25th August 2023)

The UK Expanded Access Programme (EAP): (Autumn 2016 – July 2019) >

The NICE Appraisal: Access in England (Jan 2017 – July 2019) >

Adults and Children in England who have SMA Type 3, had lost their walking ability and were ineligible for access in England (Jan 2020 – May 2021) >

Children who have SMA Type 3 in England who had Access but may have faced stopping criteria (Feb 2020 – May 2021) >

Adults in England (Feb 2020 – July 2022) >

The SMC Appraisal – Access in Scotland (Feb 2018 – May 2019) >