Scotland – Access to Risdiplam
Scotland – Access to Risdiplam
Last updated: 9th December 2024
Risdiplam may be accessed by:
- anyone with a clinical diagnosis of SMA Type 1, Type 2 or Type 3
- any pre-symptomatic infant who has SMA with one to four SMN2 copies
Our summary guides discussing all the potential treatments may be useful:
Our Treatment Update Webinars discuss latest information with health professionals.
See also: Scottish Medicines Consortium Website announcing decision in February 2022.
The licensed indication for risdiplam was updated in 2023 to remove the age restriction referred to on the SMC website to patients aged >2 months. SMC informed health boards of the change to the licence for risdiplam to include patients younger than 2 months in September 2023. See: NSD602-005.01 Medicines included in Ultra Orphan Drugs risk share arrangement.pdf
How long would it take to get to my supply started at home?
Different hospitals have different processes and timelines which can affect how long it takes for your risdiplam supply to get through the hospital system. Times may vary for how long it takes for your prescription to be finalised.
They may also vary for how long it takes for your hospital paperwork to then be referred to and reach the Homecare Company, if one is being used.
Once the Homecare Company has received your prescription and registration form from the hospital, the Company will contact you to welcome you to the service. They will answer any questions you may have and agree delivery details with you.