Drug Treatments & Screening -
What's Happening Now?
Although there’s currently no cure for SMA, this doesn’t mean that nothing can be done.
These pages tell you about any drug treatments that have been approved for use, any in the pipeline, and other related topics. Whatever the treatment, it remains vital that anyone who has SMA also has care and management as outlined in the internationally agreed Standards of Care for SMA.
Our Research Correspondents report on the available, but limited, research on rarer forms of SMA.
Programmes are beginning to be trialled in other parts of the world. In the UK, the National Screening Committee reviews whether such a programme should happen here. We submitted our views in September 2018 and are working with Genetic Alliance on a Patient Charter for access.