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NICE preparing for the review of Nusinersen and Risdiplam 

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Treatments & Research

Spinal Muscular Atrophy: A Rare but Treatable Disease of the Nervous System

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Treatments & Research

Adelphi Values Interview Study – Physical Ability: What is important to you?

Advocacy
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Resonate 2023, what a weekend!

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Research into the views of the SMA Community towards newborn screening for SMA in the UK

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Biogen Provide Update on Phase 4 RESPOND trial of Spinraza

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5-Year Results from the Nurture Spinraza Trial Published

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Treatments & Research

Scholar Rock Provide Update on Phase 2 TOPAZ trial of Apitegromab

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We are excited to share with you our brand refresh and new website!

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Say hello to Gary!

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