Skip to content

NHS England agrees to allow access to Sapphire Trial to enhance treatments for SMA

Information
Treatments & Research

England’s Managed Access Agreement for Nusinersen extended to July 2025

Information
Treatments & Research

Scholar Rock presents latest TOPAZ Trial data at the international scientific congress on SMA

Information
Treatments & Research

Food and Drug Administration (FDA) in U.S. approves Evrysdi® (Risdiplam) to include babies under 2 months old with SMA

Information
Treatments & Research