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Although there’s currently no cure for SMA, drug treatments are now available.

These pages tell you about any NHS-funded drug treatments, any in the pipeline, and other related topics. Whatever the treatment, it remains vital that anyone who has SMA also has appropriate care and management based on assessment by and discussion with their clinical team. Though some recommendations are now changing, the internationally agreed Standards of Care for SMA remains a useful reference point.

Results Published from STRONG Trial of Zolgensma

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Treatments & Research

Conversations with health professionals – new webinar!

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Treatments & Research

Interim Results from Risdiplam Jewelfish Trial Published

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Treatments & Research
Image shows test tubes in a science laboratory.

NHS England agrees to allow access to Sapphire Trial to enhance treatments for SMA

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Treatments & Research

England’s Managed Access Agreement for Nusinersen extended to July 2025

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Treatments & Research

Scholar Rock presents latest TOPAZ Trial data at the international scientific congress on SMA

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Treatments & Research

Food and Drug Administration (FDA) in U.S. approves Evrysdi® (Risdiplam) to include babies under 2 months old with SMA

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Treatments & Research