Skip to content

Although there’s currently no cure for SMA, drug treatments are now available.

These pages tell you about any NHS-funded drug treatments, any in the pipeline, and other related topics. Whatever the treatment, it remains vital that anyone who has SMA also has appropriate care and management based on assessment by and discussion with their clinical team. Though some recommendations are now changing, the internationally agreed Standards of Care for SMA remains a useful reference point.

England’s Managed Access Agreement for Nusinersen extended to July 2025

Information
Treatments & Research

Scholar Rock presents latest TOPAZ Trial data at the international scientific congress on SMA

Information
Treatments & Research

Food and Drug Administration (FDA) in U.S. approves Evrysdi® (Risdiplam) to include babies under 2 months old with SMA

Information
Treatments & Research