European Commission approves Itvisma for people aged two years and over living with 5q SMA

Treatments & Research

Advocacy

Thursday, 2 July 2026

Our CEO, Giles Lomax, recently attended the NHS ConfedExpo

Advocacy

Wednesday, 24 June 2026

We need you to write to your local MP

Advocacy

Thursday, 21 May 2026

NICE recommends nusinersen and risdiplam for permanent NHS England funding  

Advocacy

News

Thursday, 14 May 2026

Ireland Expands Newborn Screening to Include SMA and SCID

Advocacy

Monday, 13 April 2026

ISE to start screening for SMA in England from October 2026!

Advocacy

Information

News

Wednesday, 1 April 2026

A Breakthrough for Babies: Scotland Rolls Out Newborn Screening for SMA as of today!

Advocacy

News

Treatments & Research

Uncategorized

Monday, 23 March 2026

Advocating for the appointment of a National Clinical Director (NCD) for Rare Diseases

Advocacy

Monday, 9 March 2026

Rare Disease Day 2026

Advocacy

News

Thursday, 26 February 2026

Update Following the MTA Committee Meeting on SMA Treatments

Advocacy

Treatments & Research

Thursday, 5 February 2026