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News & Updates
News & Updates
Scholar Rock Provide Update on Phase 2 TOPAZ trial of Apitegromab
News
Treatments & Research
We are excited to share with you our brand refresh and new website!
News
Uncategorized
Ian, Mark, Neil & Paul’s LEJOG Challenge
Fundraising
Taking the leap for SMA UK
Fundraising
Say hello to Gary!
News
APPG for Muscular Dystrophy: Newborn Screening for Rare Conditions
Advocacy
Information
News
SMA UK Trustee Event – An evening with Sir Richard Dearlove OBE
Fundraising
News
Calling for Progress on Care Coordination in the UK
Advocacy
News
Novartis presents data on long-term treatment with Zolgensma
Information
News
Treatments & Research
Taldefgrobep Alfa Receives FDA Fast Track Designation for SMA