Interim Results from Risdiplam Jewelfish Trial Published InformationTreatments & Research Thursday, 23 February 2023
NHS England agrees to allow access to Sapphire Trial to enhance treatments for SMA InformationTreatments & Research Wednesday, 25 January 2023
England’s Managed Access Agreement for Nusinersen extended to July 2025 InformationTreatments & Research Friday, 16 December 2022
Scholar Rock presents latest TOPAZ Trial data at the international scientific congress on SMA InformationTreatments & Research Thursday, 27 October 2022
Food and Drug Administration (FDA) in U.S. approves Evrysdi® (Risdiplam) to include babies under 2 months old with SMA InformationTreatments & Research Wednesday, 1 June 2022