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5-Year Results from the Nurture Spinraza Trial Published

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Scholar Rock Provide Update on Phase 2 TOPAZ trial of Apitegromab

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We are excited to share with you our brand refresh and new website!

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Say hello to Gary!

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APPG for Muscular Dystrophy: Newborn Screening for Rare Conditions

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SMA UK Trustee Event – An evening with Sir Richard Dearlove OBE

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Calling for Progress on Care Coordination in the UK

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Novartis presents data on long-term treatment with Zolgensma

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Treatments & Research

ROCHE Community Update – SUNFISH Trial

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Treatments & Research

NHS England Provides Further Guidance around Definition of Non-Success of Zolgensma

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